5 DMD Data Readouts to Watch in 2024

Discussion in 'Pharma/Biotech Companies - In the News' started by cafead, May 6, 2024 at 11:32 AM.

  1. cafead

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    via The March approval of ITF Therapeutics’ Duvyzat marked the third new FDA-approved treatment in 10 months for Duchenne muscular dystrophy (DMD), a genetic disorder that causes progressive muscle weakness and degeneration. In June 2023, the regulator greenlit Sarepta’s Elevidys as the first-ever gene therapy for DMD. That approval was followed by Santhera Pharmaceuticals’ novel corticosteroid Agamree in October.

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