alpha-1 antitrypsin deficiency

First RNA Editing Therapy Nears Clinic as Excitement Mounts
BioSpace
Mon, 10/9/23 - 10:21 am
Wave Life Sciences
WVE-006
RNA editing
alpha-1 antitrypsin deficiency
FDA approves Krystal Biotech’s KB408 for AATD treatment
Pharmaceutical Business Review
Fri, 09/22/23 - 10:10 am
Krystal Biotech
KB408
alpha-1 antitrypsin deficiency
Centessa claims a place in the antitrypsin deficiency pipeline
EP Vantage
Wed, 11/3/21 - 10:31 am
Centessa Pharmaceuticals
alpha-1 antitrypsin deficiency
Despite Hitting Mid-Stage Trial Endpoint Goal, Vertex Strikes Out Rare Lung Disease Candidate; Stock Tumbles
Yahoo/Benzinga
Fri, 06/11/21 - 10:45 am
Vertex Pharmaceuticals
VX-864
alpha-1 antitrypsin deficiency
clinical trials