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CHAPLE disease
Regeneron’s Antibody Gets FDA Approval for Ultra-Rare Hereditary Disease
Regeneron’s Antibody Gets FDA Approval for Ultra-Rare Hereditary Disease
BioSpace
Regeneron
FDA
CHAPLE disease
Veopoz
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FDA Action Alert: Ipsen, Revance, Neurocrine and Regeneron
FDA Action Alert: Ipsen, Revance, Neurocrine and Regeneron
BioSpace
FDA
Ipsen
Revance Therapeutics
Neurocrine
Regeneron
palovarotene
fibrodysplasia ossificans progressiva
Daxxify
cervical dystonia
Ingrezza
chorea
Huntington's disease
pozelimab
CHAPLE disease
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5 Highly Anticipated FDA Decisions for Rare Diseases Coming This Year
5 Highly Anticipated FDA Decisions for Rare Diseases Coming This Year
BioSpace
Ipsen
palovarotene
fibrodysplasia ossificans progressiva
Regeneron
CHAPLE disease
pozelimab
Biomarin
Voxzogo
achondroplasia
Santhera Pharmaceuticals
vamorolone
DMD
Springworks
nirogacestat
desmoid tumors
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