Fabry disease

Chiesi starts rare diseases division, ahead of potential Fabry disease filing
Pharmaforum
Tue, 02/18/20 - 10:14 am
Chiesi
Fabry disease
Boston
R&D
Amicus widens UPenn gene therapy collaboration
Biopharma Dive
Wed, 05/29/19 - 10:35 pm
Amicus Therapeutics
UPenn
gene therapy
Galafold
Fabry disease
With new data, a biotech tries to relieve doubts about the durability of its gene therapy for Fabry disease
Stat
Wed, 02/6/19 - 09:40 am
Avrobio
Fabry disease
Amicus Finally Wins FDA Nod, Will Price Fabry Drug Below Rivals
Xconomy
Sun, 08/12/18 - 01:20 pm
Fabry disease
FDA
Amicus Therapeutics
Galafold
Amicus CEO directly lobbied FDA’s Gottlieb to reverse FDA’s rejection of migalastat, claiming a delay of up to 7 years
Endpoints
Fri, 12/15/17 - 09:33 am
Amicus
Pharma CEOs
FDA
Scott Gottlieb
migalastat
Fabry disease
Signaling a major shift at the FDA, regulators put Amicus’ once-spurned drug on fast track
Endpoints
Tue, 09/19/17 - 09:22 am
FDA
Amicus Therapeutics
migalastat
Fabry disease
fast track
FDA Reverses Decision, Allowing Amicus To File For Rare Disease Drug
Forbes
Tue, 07/11/17 - 09:53 am
FDA
Amicus Therapeutics
Rare Diseases
Fabry disease
migalastat
FDA Requests Additional Data on Amicus’ Fabry Disease Treatment
Yahoo/24-7 Wall St
Tue, 11/29/16 - 05:33 pm
Fabry disease
FDA
Amicus Therapeutics

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