gene therapy

Novartis CEO Vas Narasimhan On The Price Of Gene Therapies: 'It's A Challenge We Have To Solve'
Forbes
Thu, 11/29/18 - 11:11 am
Novartis
Pharma CEOs
Vas Narasimhan
gene therapy
AveXis
Biotech Showcase Conference Reveals Six Therapeutic Areas Receiving the Most Investment Attention in 2019
CP Wire
Tue, 11/27/18 - 12:02 pm
biotech
Alzheimer's disease
NASH
RNA
gene therapy
immuno-oncology
orphan diseases
Biotech Showcase Conference Reveals Six Therapeutic Areas Receiving the Most Investment Attention in 2019
Tue, 11/27/18 - 11:57 am
Alzheimer's disease
NASH
RNA
gene therapy
immuno-oncology
orphan diseases
Luxturna cleared for sale in Europe, but payer support uncertain
Biopharma Dive
Mon, 11/26/18 - 11:15 pm
Spark Therapeutics
Luxturna
Europe
gene therapy
Rolling up its sleeves, Axovant scoops up five gene therapy vets to propel new pipeline
Endpoints
Mon, 11/26/18 - 10:08 am
Axovant
gene therapy
Novartis/Spark’s sight gene therapy approved in EU
Pharmaforum
Fri, 11/23/18 - 01:16 pm
Novartis
Spark Therapeutics
Luxturna
gene therapy
Europe
UniQure’s hemophilia B gene therapy achieves 31% FIX activity
Fierce Biotech
Thu, 11/15/18 - 09:51 am
uniQure
hemophilia B
gene therapy
FIX-Padula
Myonexus Therapeutics Starts Trial of First-Ever Gene Therapy for Rare Type of Muscular Dystrophy
CP Wire
Thu, 11/8/18 - 12:11 pm
Myonexus
Sarepta Therapeutics
muscular dystrophy
gene therapy
Researchers Cure ALS in Laboratory Animals Using Gene Therapy
BioSpace
Wed, 11/7/18 - 10:35 am
ALS
Lou Gehrig's disease
gene therapy
University of California
San Diego
Look how far precision medicine has come
MIT Technology Review
Tue, 10/23/18 - 11:13 pm
precision medicine
personlized medicine
gene therapy
New York biotech snaps up Eli Lilly neuro veteran as CSO
Fierce Biotech
Mon, 10/15/18 - 10:40 am
Redpin Therapeutics
Eli Lilly
JLabs
gene therapy
Selecta's rapamycin nanoparticles could enable re-dosing of gene therapies
BioCentury
Fri, 10/5/18 - 09:15 pm
Selectra Biosciences
SVP-Rapamycin
nanoparticles
gene therapy
Sarepta Gene Therapy Appears To Help Fourth Boy With Duchenne Muscular Dystrophy
Forbes
Thu, 10/4/18 - 12:36 am
Sarepta Therapeutics
Duchenne Muscular Dystrophy
gene therapy
[video+transcript]Gene Therapy Could Be a Boon for This Biotech
Motley Fool
Sun, 09/30/18 - 03:38 pm
gene therapy
Rengexbio
spinal muscular atrophy
wet age-related macular degeneration
FDA lifts clinical hold on Sarepta's Duchenne MD gene therapy, clearing the way to a quick launch of a pivotal trial
Endpoints
Mon, 09/24/18 - 09:59 am
Sarepta Therapeutics
FDA
gene therapy
Duchenne Muscular Dystrophy
clinical trials
Spark/Novartis eye gene therapy nears EU market – but at what price?
Pharmaforum
Sun, 09/23/18 - 10:36 pm
Spark Therapeutics
Novartis
Luxturna
gene therapy
Europe
Amicus Therapeutics Ramps Up Gene Therapy Portfolio with Acquisition of 10 Programs
CP Wire
Thu, 09/20/18 - 09:46 am
Amicus Therapeutics
gene therapy
Batten disease
Mustang licenses immunodeficiency gene therapy from St. Jude
BioCentury
Wed, 08/15/18 - 10:58 pm
Mustang Bio
lentiviral
gene therapy
SCID
St Jude Children's Hospital
Sarepta Invests $30 Million in Gene Therapy Company
CP Wire
Mon, 08/13/18 - 11:17 am
Lacerta Therapeutics
Sarepta Therapeutics
gene therapy
RegenxBio rally fades fast after biotech reports setbacks, hospitalization in gene therapy study
Endpoints
Wed, 08/8/18 - 09:53 am
Regenxbio
gene therapy
RGX-501
clinical trials
HoFH

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