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vesleteplirsen
Sarepta pulls plug on Duchenne exon-skipping drug
Pharmaphorum
Thu, 11/7/24 - 11:09 am
Sarepta Therapeutics
Duchenne Muscular Dystrophy
DMD
vesleteplirsen
After serious side effect, Sarepta and FDA realign on next-gen Duchenne drug with trial hold lifted
Endpoints
Tue, 09/6/22 - 10:48 am
Sarepta Therapeutics
Duchenne Muscular Dystrophy
vesleteplirsen
clinical trials