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Vertex lays out plan to increase access and launch non-opioid pain reliever Journavx

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For Vertex these days, it’s all about the launches of three new products—sickle cell disease gene therapy Casgevy, the company’s fifth cystic fibrosis treatment Alyftrek and its non-opioid pain relief medication Journavx, which was approved to much fanfare by the FDA two weeks ago.

Source
Fierce Pharma

Vertex boosts cell and genetic therapies toolkit in deal worth up to $1.2bn with Arbor

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Boston-based company, Vertex, has signed a deal to use Arbor Biotechnologies’ CRISPR gene-editing technology to develop novel cell therapies for the treatment of serious diseases.

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Biopharma Reporter

New CRISPR, gene therapy results strengthen potential for treatment of blood diseases

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Three people with the inherited blood diseases sickle cell and beta thalassemia remain free of burdensome blood transfusions and their worst symptoms, months after receiving an infusion of genetically modified stem cells.

Source
BioPharma Dive