DMD

Sarepta Seeks to Strengthen Elevidys’ Case With Data in Older Kids
BioSpace
Sun, 05/18/25 - 10:41 pm
Sarepta Therapeutics
Elevidys
clinical trials
DMD
Duchenne Muscular Dystrophy
Sarepta tries to quell concerns over DMD gene therapy Elevidys as patients delay treatment after death report
Fierce Pharma
Wed, 05/7/25 - 11:25 am
Sarepta Therapeutics
DMD
Duchenne Muscular Dystrophy
earnings
Elevidys
gene therapy
Capricor Therapeutics announces completion of mid-cycle review meeting with FDA on deramiocel for the treatment of Duchenne Muscular Dystrophy cardiomyopathy
Stock Titan
Mon, 05/5/25 - 11:20 am
Capricor
DMD
DMD cardiomyopathy
FDA
deramiocel
Entrada lays off 20% of staff weeks after having FDA hold lifted
Fierce Biotech
Wed, 04/30/25 - 11:05 am
Entrada
DMD
FDA
layoffs
Sarepta and Roche aim to resume paused Elevidys trials following patient death
Clinical Trials Arena
Mon, 04/7/25 - 11:35 am
Sarepta Therapeutics
Roche
Elevidys
clinical trials
DMD
patient deaths
Sarepta’s Duchenne Gene Therapy Placed on Hold in Europe Pending Death Investigation
BioSpace
Thu, 04/3/25 - 11:26 am
Sarepta Therapeutics
Roche
gene therapy
patient deaths
Europe
Eleviys
DMD
A recent gene therapy death shines a light on AAV safety
Pharma Voice
Mon, 03/31/25 - 10:10 am
gene therapy
DMD
Sarepta Therapeutics
adeno-associated viruses
Wave's DMD drug remains on track in 48-week data ahead of FDA push next year
Fierce Biotech
Wed, 03/26/25 - 10:17 am
Wave Life Sciences
DMD
Duchenne Muscular Dystrophy
FDA
REGENXBIO reports promising gene therapy trial results
Investing.com
Wed, 03/19/25 - 11:12 pm
Regenxbio
DMD
RGX-202
Duchenne patient dies after receiving Sarepta gene therapy
BioPharma Dive
Tue, 03/18/25 - 11:32 am
Sarepta Therapeutics
DMD
Duchenne Muscular Dystrophy
Elevidys
patient deaths
PepGen pauses Phase II DMD trial to review safety data
Clinical Trials Arena
Wed, 03/5/25 - 11:57 am
PepGen
FDA
PGN-EN051
clinical trials
DMD
Duchenne Muscular Dystrophy
FDA Clears Entrada Therapeutics' Early-Stage For Potential Treatment Of Duchenne Muscular Dystrophy
Benzinga
Mon, 02/24/25 - 11:15 am
Entrada Therapeutics
ENTR-601-44
DMD
Duchenne Muscular Dystrophy
FDA
Roche reports positive topline outcomes from DMD treatment trial
Clinical Trials Arena
Tue, 01/28/25 - 10:24 am
Roche
Elevidys
DMD
gene therapy
clinical trials
Satellos doses first DMD subject in Phase Ib trial
Clinical Trials Arena
Thu, 12/12/24 - 11:26 am
Satellos Bioscience
DMD
clinical trials
SAT-3247
FDA endorses speedy approval path for Regenxbio Duchenne gene therapy
BioPharma Dive
Mon, 11/18/24 - 06:32 pm
Rengexbio
DMD
gene therapy
FDA
RGX-202
Sarepta pulls plug on Duchenne exon-skipping drug
Pharmaphorum
Thu, 11/7/24 - 11:09 am
Sarepta Therapeutics
Duchenne Muscular Dystrophy
DMD
vesleteplirsen
Pfizer lays off 75 more workers in North Carolina in wake of late-stage DMD trial fail
Fierce Pharma
Tue, 10/22/24 - 11:21 pm
Pfizer
layoffs
North Carolina
gene therapy
DMD
Capricor cell therapy improves cardiac and upper limb function in phase 2 Duchenne muscular dystrophy victory lap
Fierce Biotech
Sun, 10/13/24 - 11:27 am
Capricor
DMD
clinical trials
cell therapy
Duchenne Muscular Dystrophy
deramiocel
Wave surfs DMD success to regulators' doors, sending stock up
Fierce Biotech
Tue, 09/24/24 - 11:45 am
Wave Life Sciences
DMD
Duchenne Muscular Dystrophy
clinical trials
FDA designations boost AI-Driven cell therapy approach for Duchenne muscular dystrophy
Biopharma Reporter
Tue, 09/17/24 - 09:53 am
Somite
FDA
pediatrics
cell replacement therapy
artificial intelligence
DMD
Duchenne Muscular Dystrophy

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