Duchenne Muscular Dystrophy

earnings

Elevidys

gene therapy

Wave's DMD drug remains on track in 48-week data ahead of FDA push next year

Fierce Biotech

Wed, 03/26/25 - 10:17 am

Wave Life Sciences

Duchenne patient dies after receiving Sarepta gene therapy

BioPharma Dive

Tue, 03/18/25 - 11:32 am

Elevidys

patient deaths

PepGen pauses Phase II DMD trial to review safety data

Clinical Trials Arena

Wed, 03/5/25 - 11:57 am

FDA Clears Entrada Therapeutics' Early-Stage For Potential Treatment Of Duchenne Muscular Dystrophy

Benzinga

Mon, 02/24/25 - 11:15 am

Entrada Therapeutics

ENTR-601-44

Solid says early data suggest ‘differentiated’ Duchenne gene therapy

BioPharma Dive

Tue, 02/18/25 - 11:06 pm

Solid Biosciences

gene therapy

Sarepta pulls plug on Duchenne exon-skipping drug

Pharmaphorum

Thu, 11/7/24 - 11:09 am

vesleteplirsen

PTC Therapeutics Faces Setback on Translarna Approval

Tip Ranks

Fri, 10/18/24 - 11:31 am

Capricor cell therapy improves cardiac and upper limb function in phase 2 Duchenne muscular dystrophy victory lap

Fierce Biotech

Sun, 10/13/24 - 11:27 am

deramiocel

Wave surfs DMD success to regulators' doors, sending stock up

Fierce Biotech

Tue, 09/24/24 - 11:45 am

Wave Life Sciences

clinical trials

FDA designations boost AI-Driven cell therapy approach for Duchenne muscular dystrophy

Biopharma Reporter

Tue, 09/17/24 - 09:53 am

Somite

pediatrics

cell replacement therapy

artificial intelligence

DMD clinical studies evolve with emphasis on building designs around relevant endpoints

Clinical Trials Arena

Fri, 08/30/24 - 11:24 am

clinical trials

Pfizer gene therapy for Duchenne fails to meet goals of key trial

BioPharma Dive

Wed, 06/12/24 - 11:32 pm

Pfizer

clinical trials

Ciffreo

FDA approves Italfarmaco’s Duvyzat for DMD treatment

Pharmaceutical Business Review

Fri, 03/22/24 - 09:38 am

Regenxbio data suggest ‘niche’ in Duchenne gene therapy

BioPharma Dive

Thu, 03/7/24 - 11:05 am

Regenxbio

Sarepta’s Duchenne Gene Therapy Elevidys Nabs $200M on Strong Demand

BioSpace

Thu, 02/29/24 - 11:00 am

FDA to review Sarepta's Duchenne gene therapy for traditional approval

Reuters

Fri, 02/16/24 - 11:38 am

gene therapy

Elevidys

Santhera debuts DMD drug Agamree in Germany

Pharmaphorum

Mon, 01/15/24 - 09:37 am

Santhera

myotonic muscular dystrophy

Agamree

Germany

Dyne's shares surge after promising data on muscle disorder treatment

Reuters

Wed, 01/3/24 - 09:33 am

Dyne Therapeutics

clinial trials

DYNE-101

FDA rebuffs Entrada's attempt to get yearlong hold on DMD drug lifted

Fierce Biotech

Wed, 11/22/23 - 12:03 pm

Entrada Therapeutics