Duchenne Muscular Dystrophy

FDA Lifts Clinical Hold on Solid Biosciences’ DMD Gene Therapy Trial
BioSpace
Thu, 10/1/20 - 11:08 pm
Solid Biosciences
FDA
clinical trials
gene therapy
Duchenne Muscular Dystrophy
New data bolsters Sarepta gene therapies for two deadly muscle diseases
Biopharma Dive
Mon, 09/28/20 - 10:45 am
Sarepta Therapeutics
gene therapy
Duchenne Muscular Dystrophy
Limb Girdle Muscular Dystrophy
SRP-9001
SRP-9003
Sarepta faces another gene therapy hiccup as Regenxbio sues over Jim Wilson's patent
Endpoints
Thu, 09/17/20 - 10:40 am
Sarepta Therapeutics
gene therapy
Regenxbio
Duchenne Muscular Dystrophy
Sarepta cites 'overburdened' FDA as factor in DMD gene therapy delay
Fierce Biotech
Fri, 09/11/20 - 10:55 am
Sarepta Therapeutics
Duchenne Muscular Dystrophy
gene therapy
FDA
Sarepta shares fall on potential regulatory delay for experimental Duchenne drug
Marketwatch
Thu, 09/10/20 - 10:21 am
Sarepta Therapeutics
Duchenne Muscular Dystrophy
SRP-9001
Santhera bags DMD drug in 3-way deal with Idorsia and ReveraGen
Fierce Biotech
Wed, 09/2/20 - 11:04 am
Santhera
vamorolone
Duchenne Muscular Dystrophy
Idorsia
ReveraGen
Sarepta Therapeutics Gets Fast-Track FDA Review For Muscular Dystrophy Drug
Investors Business Daily
Tue, 08/25/20 - 10:00 pm
Sarepta Therapeutics
FDA
fast track
Duchenne Muscular Dystrophy
casimersen
FDA gives speedy approval to another Duchenne drug
BioPharma Dive
Wed, 08/12/20 - 11:58 pm
FDA
NS Pharma
Japan
Duchenne Muscular Dystrophy
Viltepso
viltolarsen
FDA keeps Solid Bio's troubled Duchenne MD gene therapy on clinical lockdown in latest setback
Endpoints
Mon, 07/27/20 - 11:05 am
Solid Biosciences
Duchenne Muscular Dystrophy
FDA
gene therapy
5 FDA approval decisions to watch in the 3rd quarter
BioPharma Dive
Thu, 07/9/20 - 11:09 am
FDA
Gilead Sciences
filgotinib
rheumatoid arthritis
GSK
belantamab mafodotin
Multiple Myeloma
NS Pharma
viltolarsen
Duchenne Muscular Dystrophy
Sarepta bags drug to fully unlock DMD gene therapy opportunity
Fierce Biotech
Thu, 07/2/20 - 11:19 am
Sarepta Therapeutics
Duchenne Muscular Dystrophy
Hansa Biopharma
gene therapy
OptumRx: The 3 drugs that will have the biggest impact on payers, patients in 2020
Beckers Hospital Review
Thu, 06/11/20 - 10:46 pm
OptumRx
Roche
PTC Therapeutics
risdiplam
SMA
NS Pharma
viltolarsen
Duchenne Muscular Dystrophy
Immunomedics
Trodelvy
triple negative breast cancer
Safety questions linger as Pfizer preps Duchenne gene therapy for final test
BioPharma Dive
Fri, 05/15/20 - 10:20 am
Pfizer
gene therapy
Duchenne Muscular Dystrophy
PF-06939926
One year on, Capricor's stem cell therapy appears to help DMD patients in small study, but investors balk at the data
Endpoints
Wed, 05/13/20 - 11:28 am
Capricor
stem cells
Duchenne Muscular Dystrophy
CAP-1002
Wave Life Sciences hits tumultuous waters as ax comes crashing down on staffers
Fierce Biotech
Mon, 02/10/20 - 10:31 am
Wave Life Sciences
layoffs
Duchenne Muscular Dystrophy
FDA Flags Risk of Infection, Kidney Damage for Sarepta Duchenne Drugs
Xconomy
Wed, 01/22/20 - 06:41 pm
Sarepta Therapeutics
Vyondys 53
Duchenne Muscular Dystrophy
FDA
Solid Bio Restructures to Get Halted Gene Therapy Study Back on Track
Xconomy
Thu, 01/9/20 - 10:35 am
Solid Biosciences
gene therapy
reorganization
Duchenne Muscular Dystrophy
Roche Puts Up Historic $1.15B for Sarepta Duchenne Gene Therapy Deal
Xconomy
Tue, 12/24/19 - 12:00 am
Roche
Sarepta Therapeutics
FDA
Duchenne Muscular Dystrophy
SRP-9001
Wave Stock Crashes After Decision to Halt Duchenne Drug Studies
Xconomy
Mon, 12/16/19 - 10:35 pm
Wave Life Sciences
Duchenne Muscular Dystrophy
suvodirsen
clinical trials
3 Biotech Stocks With Big Incoming Catalysts
Motley Fool
Mon, 12/16/19 - 10:52 am
Axsome Therapeutics
AXS-05
Solid Biosciences
SGT-001
Duchenne Muscular Dystrophy
major depressive disorder
Intra-Cellular Therapies
lumateperone
schizophrenia

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