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» base editing
base editing
Beam base editing therapy gets ‘proof of concept’ in rare lung disease
BioPharma Dive
Mon, 03/10/25 - 11:17 pm
Beam Therapeutics
base editing
alpha-1 antitrypsin deficiency
CRISPR
Beam hits hemoglobin goal in first base editing clinical data, reports death tied to conditioning drug
Fierce Biotech
Tue, 11/5/24 - 10:05 am
Beam Therapeutics
clinical trials
sickle cell disease
CRISPR
base editing
Study: Base Editing Shows Promise In Treating Heart Disease
BioSpace
Tue, 01/17/23 - 10:28 am
gene editing
base editing
heart disease
heart damage